Sickle Cell Disease

Akums Drugs gets patent for formulation to manage sickle cell disease

Akums Drugs and Pharmaceuticals on Friday said it has received patent for a formulation for Sickle Cell Disease (SCD). The company has received a patent from India patent office for its room temperature stable oral suspension of Hydroxyurea, a formulation aimed at managing SCD. "Our constant endeavor is to work on affordable medicines for Orphan Drugs and reduce dependency on imported medicines ensuring patient safety from rare diseases with timely and necessary treatment," Akums Managing Director Sanjeev Jain said in a statement. SCD, a genetic blood disorder, leads to severe health complications such as anaemia, frequent pain episodes and other debilitating symptoms, affecting millions worldwide, especially in India and Africa. Akums said its formulation will come at a fraction of the cost of imported Hydroxyurea solution.

ICMR to conduct first Chintan Shivir for sickle cell disease research

New Delhi [India], September 4 (ANI): The Indian Council for Medical Research (ICMR) is scheduled to organise the first brainstorming session on sickle cell disease research for two days.The top scientists and medical experts all over the country will participate in the Chintan Shivir to be held from September 5 to September 6, 2024.According to the sources, the purpose behind organising the brainstorming session is to identify the research, diagnosis and affordable treatment for sickle cell disease."We want to identify the research properties that can be taken up in sickle cell disease and existing scenarios with respect to the screening , the diagnosis, treatment, preventive measuresand awareness," said sources.During two days, panel discussion will have six different sessions, like patient perspectives understanding the patients living with SCD and their needs, strategic open brainstorming, screening methods & strategies, antenatal and newborn screening point of care tests, ..

Novo Nordisk plans to introduce drug for sickle cell disease in 3-5 years

The company announced the plan to hire about 1,300 new employees by the end of 2026, as per the statement at a media briefing

Akums introduces room temperature treatment for sickle cell disease

sickle cell disease is a genetic blood disorder that causes severe pain and complications. It is particularly prevalent among tribal populations in India

First gene-editing therapy for sickle cell disease approved by US FDA

The agency approved Lyfgenia from bluebird bio, and a separate treatment called Casgevy by partners Vertex Pharmaceuticals and Crispr Therapeutics

Cost to cut sickle cell disease's risk beyond reach of most Indians: Lancet

The costs required to reduce the risk of sickle cell disease is beyond the reach of most individuals in India and sub-Saharan Africa, where the disease is most prevalent, says a new Commission published in The Lancet Haematology journal. The Commission publishes shortly after a recent study in the same journal found that the highest burden of sickle cell disease (SCD) disability was concentrated in western and central sub-Saharan Africa and India. The authors of the Commission also noted that there is a shortage of healthcare and scientific professionals with expertise in SCD, as well as a lack of trials aimed at developing novel treatments in these countries. SCD is a group of inherited red blood cell disorders that affect hemoglobin, the protein that carries oxygen through the body. The condition affects more than 20 million people worldwide. The recent study suggested there were 376,000 (3.76 lakh) global SCD-related deaths in 2021, compared to 34,400 cause-specific ...

PM launches sickle cell anemia eradication mission 2047; slams Cong

Prime Minister Narendra Modi on Saturday launched National Sickle Cell Anemia Eradication Mission 2047 by unveiling a portal and also released a guideline for the management of the disease and different modules for its monitoring. At a function held at Shahdol in Madhya Pradesh, the prime minister took a swipe at the opposition and asked people to beware of "fake guarantees" being given by "family-centric" political parties including Congress. Beware of those (parties) who are giving fake guarantees. Such people have brought schemes of guarantees despite they don't have their own (political) guarantee, Modi said. He said, "Family-centric parties including Congress are hobnobbing together". On the occasion, Modi started the distribution of more than 3 crore digital Ayushman cards in the country and one crore PVC Ayushman Bharat cards in MP. He announced that Rani Durgavati's 500th birth anniversary will be celebrated across India and stamps will be released. The prime minister ...

PM Modi to visit MP on Tuesday; flag off five Vande Bharat trains

Prime Minister Narendra Modi will be on a day-long visit to Madhya Pradesh on June 27 during which he will flag off five Vande Bharat trains and launch the National Sickle Cell Anaemia Elimination Mission, his office said on Monday. The prime minister will reach Rani Kamalapati railway station around 10:30 am and flag off five Vande Bharat trains, a statement issued by the Prime Minister's Office (PMO) said. Modi will attend a public programme in Shahdol district around 3 pm. He will honour Rani Durgavati, who ruled Gondwana in the mid-16th century; launch the National Sickle Cell Anaemia Elimination Mission and kickstart distribution of Ayushman cards. He will also visit Pakaria village in Shahdol, according to the statement. The five Vande Bharat trains that Modi will flag off are -- Rani Kamalapati-Jabalpur Vande Bharat Express, Khajuraho-Bhopal-Indore Vande Bharat Express, Madgaon (Goa)-Mumbai Vande Bharat Express, Dharwad-Bengaluru Vande Bharat Express, and Hatia-Patna Vande .

Elimination of sickle cell disease a multi-sectoral mission: VK Paul

He said that elimination of the disease is an integral part of achieving the holistic vision of health for all in India

World-first gene therapy cures teen with sickle cell disease

Sickle cell is caused by an error in instructions for making haemoglobin, which is packed into RBC